Sfoglia per Autore
Pleckstrin-2 is essential for erythropoiesis in β-thalassemic mice, reducing apoptosis and enhancing enucleation
2021-01-01 Feola, M.; Zamperone, A.; Moskop, D.; Chen, H.; Casu, C.; Lama, D.; Di Martino, J.; Djedaini, M.; Papa, L.; Martinez, M. R.; Choesang, T.; Bravo-Cordero, J. J.; Mackay, M.; Zumbo, P.; Brinkman, N.; Abrams, C. S.; Rivella, S.; Hattangadi, S.; Mason, C. E.; Hoffman, R.; Ji, P.; Follenzi, A.; Ginzburg, Y. Z.
Deciphering the Ets-1/2-mediated transcriptional regulation of F8 gene identifies a minimal F8 promoter for hemophilia A gene therapy
2021-01-01 Famà, Rosella; Borroni, Ester; Merlin, Simone; Airoldi, Chiara; Pignani, Silvia; Cucci, Alessia; Corà, Davide; Bruscaggin, Valentina; Scardellato, Sharon; Faletti, Stefania; Pelicci, Giuliana; Pinotti, Mirko; Walker, Gillian E; Follenzi, Antonia
Identification and functional characterization of a novel splicing variant in the F8 coagulation gene causing severe hemophilia A
2020-01-01 Famà, Rosella; Borroni, Ester; Zanolini, Diego; Merlin, Simone; Bruscaggin, Valentina; Walker, Gillian E; Olgasi, Cristina; Babu, Deepak; Agnelli Giacchello, Jacopo; Valeri, Federica; Giordano, Mara; Borchiellini, Alessandra; Follenzi, Antonia
Regulatory-Compliant Validation of a Highly Sensitive qPCR for Biodistribution Assessment of Hemophilia A Patient Cells
2020-01-01 Bittorf, P.; Bergmann, T.; Merlin, S.; Olgasi, C.; Pullig, O.; Sanzenbacher, R.; Zierau, M.; Walles, H.; Follenzi, A.; Braspenning, J.
Ipsc-derived liver organoids: A journey from drug screening, to disease modeling, arriving to regenerative medicine
2020-01-01 Olgasi, C.; Cucci, A.; Follenzi, A.
Multiparameter flow cytometric detection and quantification of senescent cells in vitro
2020-01-01 Adewoye, A. B.; Tampakis, D.; Follenzi, A.; Stolzing, A.
Escape or Fight: Inhibitors in Hemophilia A
2020-01-01 Merlin, S.; Follenzi, A.
Thyroid hormone inhibits hepatocellular carcinoma progression via induction of differentiation and metabolic reprogramming
2020-01-01 Kowalik, M. A.; Puliga, E.; Cabras, L.; Sulas, P.; Petrelli, A.; Perra, A.; Ledda-Columbano, G. M.; Morandi, A.; Merlin, S.; Orru, C.; Sanchez-Martin, C.; Fornari, F.; Gramantieri, L.; Parri, M.; Rasola, A.; Bellomo, S. E.; Sebastian, C.; Follenzi, A.; Giordano, S.; Columbano, A.
Flow-Cytometry Platform for Intracellular Detection of FVIII in Blood Cells: A New Tool to Assess Gene Therapy Efficiency for Hemophilia A
2020-01-01 Elnaggar, M.; Al-Mohannadi, A.; Kizhakayil, D.; Raynaud, C. M.; Al-Mannai, S.; Gentilcore, G.; Pavlovski, I.; Sathappan, A.; Van Panhuys, N.; Borsotti, C.; Follenzi, A.; Grivel, J. -C.; Deola, S.
Biological and clinical implications of BIRC3 mutations in chronic lymphocytic leukemia
2020-01-01 Diop, Fary; Moia, Riccardo; Favini, Chiara; Spaccarotella, Elisa; De Paoli, Lorenzo; Bruscaggin, Alessio; Spina, Valeria; Terzi-di-Bergamo, Lodovico; Arruga, Francesca; Tarantelli, Chiara; Deambrogi, Clara; Rasi, Silvia; Adhinaveni, Ramesh; Patriarca, Andrea; Favini, Simone; Sagiraju, Sruthi; Jabangwe, Clive; Kodipad, Ahad A; Peroni, Denise; Mauro, Francesca R; Del Giudice, Ilaria; Forconi, Francesco; Cortelezzi, Agostino; Zaja, Francesco; Bomben, Riccardo; Rossi, Francesca Maria; Visco, Carlo; Chiarenza, Annalisa; Rigolin, Gian Matteo; Marasca, Roberto; Coscia, Marta; Perbellini, Omar; Tedeschi, Alessandra; Laurenti, Luca; Motta, Marina; Donaldson, David; Weir, Phil; Mills, Ken; Thornton, Patrick; Lawless, Sarah; Bertoni, Francesco; Del Poeta, Giovanni; Cuneo, Antonio; Follenzi, Antonia; Gattei, Valter; Boldorini, Renzo Luciano; Catherwood, Mark; Deaglio, Silvia; Foá, Robin; Gaidano, Gianluca; Rossi, Davide
Transcriptional Targeting and MicroRNA Regulation of Lentiviral Vectors
2019-01-01 Merlin, Simone; Follenzi, Antonia
Insulin-producing organoids engineered from islet and amniotic epithelial cells to treat diabetes
2019-01-01 Lebreton, F.; Lavallard, V.; Bellofatto, K.; Bonnet, R.; Wassmer, C. H.; Perez, L.; Kalandadze, V.; Follenzi, A.; Boulvain, M.; Kerr-Conte, J.; Goodman, D. J.; Bosco, D.; Berney, T.; Berishvili, E.
Tailoring the CRISPR system to transactivate coagulation gene promoters in normal and mutated contexts
2019-01-01 Pignani, S.; Zappaterra, F.; Barbon, E.; Follenzi, A.; Bovolenta, M.; Bernardi, F.; Branchini, A.; Pinotti, M.
Tumor Targeting by Monoclonal Antibody Functionalized Magnetic Nanoparticles
2019-01-01 Oltolina, Francesca; Colangelo, Donato; Miletto, Ivana; Clemente, Nausicaa; Miola, Marta; Verné, Enrica; Prat, Maria; Follenzi, Antonia
FVIII expression by its native promoter sustains long-term correction avoiding immune response in hemophilic mice
2019-01-01 Merlin, Simone; Famà, Rosella; Borroni, Ester; Zanolini, Diego; Bruscaggin, Valentina; Zucchelli, Silvia; Follenzi, Antonia
Fetuin B Links Vitamin D deficiency and Pediatric Obesity: Direct Negative Regulation by Vitamin D.
2018-01-01 Walker, Ge; Follenzi, A; Bruscaggin, Valentina; Manfredi, M; Bellone, S; Marengo, E; Maiuri, L; Prodam, F; Bona, G
PPARs are mediators of anti-cancer properties of superparamagnetic iron oxide nanoparticles (SPIONs) functionalized with conjugated linoleic acid
2018-01-01 Ricci, Marina; Miola, Marta; Multari, Cristina; Borroni, Ester; Canuto, Rosa Angela; Congiusta, Noemi; Vernè, Enrica; Follenzi, Antonia; Muzio, Giuliana
Emerging Therapeutic Approaches for Diamond Blackfan Anemia
2018-01-01 Aspesi, Anna; Borsotti, Chiara; Follenzi, Antonia
Patient-Specific iPSC-Derived Endothelial Cells Provide Long-Term Phenotypic Correction of Hemophilia A
2018-01-01 Olgasi, C; Talmon, M; Merlin, S; Cucci, Alessia; Richaud-Patin, Y; Ranaldo, G; Colangelo, D; Di Scipio, F; Berta, Gn; Borsotti, C; Valeri, F; Faraldi, F; Prat, M; Messina, M; Schinco, P; Lombardo, A; Raya, A; Follenzi, A.
A humanized mouse model of liver fibrosis following expansion of transplanted hepatic stellate cells
2018-01-01 Benten, Daniel; Kluwe, Johannes; Wirth, Jan W.; Thiele, Nina D.; Follenzi, Antonia; Bhargava, Kuldeep K.; Palestro, Christopher J.; Koepke, Michael; Tjandra, Reni; Volz, Tassilo; Lutgehetmann, Marc; Gupta, Sanjeev
Titolo | Data di pubblicazione | Autore(i) | File |
---|---|---|---|
Pleckstrin-2 is essential for erythropoiesis in β-thalassemic mice, reducing apoptosis and enhancing enucleation | 1-gen-2021 | Feola, M.; Zamperone, A.; Moskop, D.; Chen, H.; Casu, C.; Lama, D.; Di Martino, J.; Djedaini, M.; Papa, L.; Martinez, M. R.; Choesang, T.; Bravo-Cordero, J. J.; Mackay, M.; Zumbo, P.; Brinkman, N.; Abrams, C. S.; Rivella, S.; Hattangadi, S.; Mason, C. E.; Hoffman, R.; Ji, P.; Follenzi, A.; Ginzburg, Y. Z. | |
Deciphering the Ets-1/2-mediated transcriptional regulation of F8 gene identifies a minimal F8 promoter for hemophilia A gene therapy | 1-gen-2021 | Famà, Rosella; Borroni, Ester; Merlin, Simone; Airoldi, Chiara; Pignani, Silvia; Cucci, Alessia; Corà, Davide; Bruscaggin, Valentina; Scardellato, Sharon; Faletti, Stefania; Pelicci, Giuliana; Pinotti, Mirko; Walker, Gillian E; Follenzi, Antonia | |
Identification and functional characterization of a novel splicing variant in the F8 coagulation gene causing severe hemophilia A | 1-gen-2020 | Famà, Rosella; Borroni, Ester; Zanolini, Diego; Merlin, Simone; Bruscaggin, Valentina; Walker, Gillian E; Olgasi, Cristina; Babu, Deepak; Agnelli Giacchello, Jacopo; Valeri, Federica; Giordano, Mara; Borchiellini, Alessandra; Follenzi, Antonia | |
Regulatory-Compliant Validation of a Highly Sensitive qPCR for Biodistribution Assessment of Hemophilia A Patient Cells | 1-gen-2020 | Bittorf, P.; Bergmann, T.; Merlin, S.; Olgasi, C.; Pullig, O.; Sanzenbacher, R.; Zierau, M.; Walles, H.; Follenzi, A.; Braspenning, J. | |
Ipsc-derived liver organoids: A journey from drug screening, to disease modeling, arriving to regenerative medicine | 1-gen-2020 | Olgasi, C.; Cucci, A.; Follenzi, A. | |
Multiparameter flow cytometric detection and quantification of senescent cells in vitro | 1-gen-2020 | Adewoye, A. B.; Tampakis, D.; Follenzi, A.; Stolzing, A. | |
Escape or Fight: Inhibitors in Hemophilia A | 1-gen-2020 | Merlin, S.; Follenzi, A. | |
Thyroid hormone inhibits hepatocellular carcinoma progression via induction of differentiation and metabolic reprogramming | 1-gen-2020 | Kowalik, M. A.; Puliga, E.; Cabras, L.; Sulas, P.; Petrelli, A.; Perra, A.; Ledda-Columbano, G. M.; Morandi, A.; Merlin, S.; Orru, C.; Sanchez-Martin, C.; Fornari, F.; Gramantieri, L.; Parri, M.; Rasola, A.; Bellomo, S. E.; Sebastian, C.; Follenzi, A.; Giordano, S.; Columbano, A. | |
Flow-Cytometry Platform for Intracellular Detection of FVIII in Blood Cells: A New Tool to Assess Gene Therapy Efficiency for Hemophilia A | 1-gen-2020 | Elnaggar, M.; Al-Mohannadi, A.; Kizhakayil, D.; Raynaud, C. M.; Al-Mannai, S.; Gentilcore, G.; Pavlovski, I.; Sathappan, A.; Van Panhuys, N.; Borsotti, C.; Follenzi, A.; Grivel, J. -C.; Deola, S. | |
Biological and clinical implications of BIRC3 mutations in chronic lymphocytic leukemia | 1-gen-2020 | Diop, Fary; Moia, Riccardo; Favini, Chiara; Spaccarotella, Elisa; De Paoli, Lorenzo; Bruscaggin, Alessio; Spina, Valeria; Terzi-di-Bergamo, Lodovico; Arruga, Francesca; Tarantelli, Chiara; Deambrogi, Clara; Rasi, Silvia; Adhinaveni, Ramesh; Patriarca, Andrea; Favini, Simone; Sagiraju, Sruthi; Jabangwe, Clive; Kodipad, Ahad A; Peroni, Denise; Mauro, Francesca R; Del Giudice, Ilaria; Forconi, Francesco; Cortelezzi, Agostino; Zaja, Francesco; Bomben, Riccardo; Rossi, Francesca Maria; Visco, Carlo; Chiarenza, Annalisa; Rigolin, Gian Matteo; Marasca, Roberto; Coscia, Marta; Perbellini, Omar; Tedeschi, Alessandra; Laurenti, Luca; Motta, Marina; Donaldson, David; Weir, Phil; Mills, Ken; Thornton, Patrick; Lawless, Sarah; Bertoni, Francesco; Del Poeta, Giovanni; Cuneo, Antonio; Follenzi, Antonia; Gattei, Valter; Boldorini, Renzo Luciano; Catherwood, Mark; Deaglio, Silvia; Foá, Robin; Gaidano, Gianluca; Rossi, Davide | |
Transcriptional Targeting and MicroRNA Regulation of Lentiviral Vectors | 1-gen-2019 | Merlin, Simone; Follenzi, Antonia | |
Insulin-producing organoids engineered from islet and amniotic epithelial cells to treat diabetes | 1-gen-2019 | Lebreton, F.; Lavallard, V.; Bellofatto, K.; Bonnet, R.; Wassmer, C. H.; Perez, L.; Kalandadze, V.; Follenzi, A.; Boulvain, M.; Kerr-Conte, J.; Goodman, D. J.; Bosco, D.; Berney, T.; Berishvili, E. | |
Tailoring the CRISPR system to transactivate coagulation gene promoters in normal and mutated contexts | 1-gen-2019 | Pignani, S.; Zappaterra, F.; Barbon, E.; Follenzi, A.; Bovolenta, M.; Bernardi, F.; Branchini, A.; Pinotti, M. | |
Tumor Targeting by Monoclonal Antibody Functionalized Magnetic Nanoparticles | 1-gen-2019 | Oltolina, Francesca; Colangelo, Donato; Miletto, Ivana; Clemente, Nausicaa; Miola, Marta; Verné, Enrica; Prat, Maria; Follenzi, Antonia | |
FVIII expression by its native promoter sustains long-term correction avoiding immune response in hemophilic mice | 1-gen-2019 | Merlin, Simone; Famà, Rosella; Borroni, Ester; Zanolini, Diego; Bruscaggin, Valentina; Zucchelli, Silvia; Follenzi, Antonia | |
Fetuin B Links Vitamin D deficiency and Pediatric Obesity: Direct Negative Regulation by Vitamin D. | 1-gen-2018 | Walker, Ge; Follenzi, A; Bruscaggin, Valentina; Manfredi, M; Bellone, S; Marengo, E; Maiuri, L; Prodam, F; Bona, G | |
PPARs are mediators of anti-cancer properties of superparamagnetic iron oxide nanoparticles (SPIONs) functionalized with conjugated linoleic acid | 1-gen-2018 | Ricci, Marina; Miola, Marta; Multari, Cristina; Borroni, Ester; Canuto, Rosa Angela; Congiusta, Noemi; Vernè, Enrica; Follenzi, Antonia; Muzio, Giuliana | |
Emerging Therapeutic Approaches for Diamond Blackfan Anemia | 1-gen-2018 | Aspesi, Anna; Borsotti, Chiara; Follenzi, Antonia | |
Patient-Specific iPSC-Derived Endothelial Cells Provide Long-Term Phenotypic Correction of Hemophilia A | 1-gen-2018 | Olgasi, C; Talmon, M; Merlin, S; Cucci, Alessia; Richaud-Patin, Y; Ranaldo, G; Colangelo, D; Di Scipio, F; Berta, Gn; Borsotti, C; Valeri, F; Faraldi, F; Prat, M; Messina, M; Schinco, P; Lombardo, A; Raya, A; Follenzi, A. | |
A humanized mouse model of liver fibrosis following expansion of transplanted hepatic stellate cells | 1-gen-2018 | Benten, Daniel; Kluwe, Johannes; Wirth, Jan W.; Thiele, Nina D.; Follenzi, Antonia; Bhargava, Kuldeep K.; Palestro, Christopher J.; Koepke, Michael; Tjandra, Reni; Volz, Tassilo; Lutgehetmann, Marc; Gupta, Sanjeev |
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